Mucopolysaccharidosis IV - 18 Studies Found

Completed : Psychological Concomitants of Morquio Syndrome (The MAP Study)
:
  • Morquio Disease
  • Mucopolysaccharidosis IV<
    : 2012-12-13
Terminated : Morquio's Syndrome: a Case Study
: Morquio's Disease
: 2008-01-25
: Other: physiotherapeutic treatment At first, the patient was submitted to a conventional physiotherapeut
Recruiting : Pregnancy With Morquio Syndrome - What Are Patients' Perspectives and Has ERT Changed Them?
:
  • Morquio Disease
  • MPS - Mucopolysaccharidosis

: 2017-05-10
: Other: Interview In-person or telephone in-depth interview
Active, not recruiting : Psychological Concomitants of Morquio A Syndrome - Longitudinal Effects of Enzyme Replacement Therapy (The MAPLE Study)
:
  • Morquio A Syndrome
  • Mucopolysaccharidosis IV A

: 2014-08-01
Withdrawn : Dynamic Gait Analysis in Children With Mucopolysaccharidosis Type IVa
:
  • Mucopolysaccharidosis IV
  • Morquio A Disease

: 2014-05-28
Completed : Screening an Orthopedic Population for Mildly-affected Individuals With Morquio Syndrome A and Maroteaux-Lamy Syndrome
:
  • Morquio Syndrome A
  • Maroteaux Lamy Syndrome
  • MPS IVA
  • Morquio Syndrome

: 2013-08-08
Recruiting : A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
:
  • Mucopolysaccharidosis IV Type A
  • Morquio A Syndrome
  • : 2014-10-28
    : Drug: Vimizim® (elosulfase alfa) Recombinant human N acetylgalactosamine 6 sulfatase (rhGALNS)
Completed : Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
:
  • Mucopolysaccharidosis IV A
  • Morquio A Syndrome
  • Drug: BMN 110 - Weekly

Terminated : A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
:
  • MPS IV A
  • Mucopolysaccharidosis IVA
  • Morquio A Syndrome

    • : 2008-11-06
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