Mucopolysaccharidoses - 25 Studies Found
Active, not recruiting |
: Safety and Dose Ranging Study of Insulin Receptor MAb-IDUA Fusion Protein in Patients With MPS I : Mucopolysaccharidosis I : 2015-02-19 : Drug: AGT-181 (HIRMAb-IDUA) intravenous infusion over 3-4 hours |
Completed |
: To Evaluate the Safety and Efficacy of GC1111 (Recombinant Human Iduronate-2-sulfatase) in Hunter Syndrome Patients : Mucopolysaccharidosis II : 2011-02-22 :
|
Not yet recruiting |
: Study of Idursulfase-beta (GC1111) in Hunter Syndrome : Mucopolysaccharidosis II : 2016-01-17 :
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Recruiting |
: Safety and Dose Ranging Study of Insulin Receptor MoAb-IDS Fusion Protein in Patients With Hunter Syndrome : Mucopolysaccharidosis II : 2014-10-02 : Drug: AGT-182 Recombinant HIRMAb-IDS |
Recruiting |
: Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP) : Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) : 2005-09-13 |